WebGalafold is a medicine used to treat patients aged 12 years and above who have Fabry disease. This is a rare inherited disorder where patients have various mutations … WebSep 13, 2024 · Summary. Amicus Therapeutics is a highly promising grower that's powered by multiple catalysts. Galafold is now approved for commercialization worldwide. …
GALAFOLD® Information for Healthcare Professionals
WebGALAFOLD is indicated for the treatment of adults with a confirmed diagnosis of Fabry disease and an amenable galactosidase alpha gene ( GLA ) variant based on in vitro … WebAug 27, 2024 · This website only confirms the amenability of a GLA gene mutation to Galafold®, as determined by the Migalastat GLP HEK Assay. Detailed results from the Migalastat GLP HEK Assay are available for all amenable GLA mutations. Please contact Amicus Medical Information and provide the mutation using standard HGVS nomenclature. timewalking mage tower appearances
Amicus Therapeutics Announces European Commission …
WebGalafold Fabry Disease AMICUS ASSIST ® (patient support program) Other By submitting your information, you agree that the information you provide may be used by Amicus Therapeutics, Inc., its affiliates, and third parties working on behalf of Amicus Therapeutics to respond to your request and to provide you with additional communications about ... WebTo reach Amicus Assist® for product assistance and support, please call us toll-free, Monday through Friday, from 8am to 8pm ET at 1-833-AMICUS-A (1-833-264-2872) If you have questions or concerns about Galafold or the MyDay app, or you need to report medication side effects or adverse events, contact Amicus Therapeutics at 1-877-4 … WebIn order to break down fatty substances, alpha-Gal A needs to travel into the lysosome. But usually only properly folded enzymes make it into this part of the cell. Misfolded enzymes, like some of those seen in Fabry disease, cannot enter the lysosome and are broken down instead. For adults with an amenable gene variant, that’s where Galafold ... timewalking mage tower location